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Gene Therapy
Hearing Loss
Breakthrough Gene Therapy Enables Infant Born Deaf to Hear
Physician’s Briefing Staff
May 10, 2024
2 min read
Child Health
Baby Girl Born Deaf Gains Hearing After Gene Therapy
Ernie Mundell
May 10, 2024
3 min read
Eye Care
Gene Therapy Improves Vision in People With Inherited Blindness
Dennis Thompson
May 06, 2024
3 min read
Neurology
Intrathecal Gene Therapy Shows Promise in Giant Axonal Neuropathy
Elana Gotkine
Mar 25, 2024
2 min read
Neurology
First Gene Therapy for Children With Metachromatic Leukodystrophy Approved by FDA
Lori Solomon
Mar 22, 2024
1 min read
Hearing Loss
Gene Therapy Brings Hearing to Kids With Congenital Deafness
Dennis Thompson
Jan 25, 2024
3 min read
Blood Disorders
Gene Therapy for Sickle Cell Disease Likely Cost-Effective at <$2 Million
Elana Gotkine
Jan 22, 2024
1 min read
Blood Disorders
First Gene-Editing Therapies for Sickle Cell Disease Approved by FDA
Physician’s Briefing Staff
Dec 08, 2023
2 min read
General Health
FDA Approves Landmark Sickle Cell Gene Therapies
Dennis Thompson
Dec 08, 2023
4 min read
Read More
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