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Genetic Disorders
Blood Disorders
Oral Engasertib Safe for Hereditary Hemorrhagic Telangiectasia
Elana Gotkine
Dec 04, 2025
2 min read
Ear Nose and Throat
Adenotonsillectomy Safe in Children With Down Syndrome, Other Genetic Syndromes
Elana Gotkine
Nov 26, 2025
1 min read
Cardiovascular Diseases
Most People Aren't Aware Of Genetic Risk For Dangerously High Cholesterol
Dennis Thompson
Nov 21, 2025
2 min read
Child Health
Lentiviral Gene Therapy Shows Sustained Clinical Efficacy for ADA-SCID
Elana Gotkine
Oct 17, 2025
2 min read
Child Health
World Record Set For Fastest Genome Sequencing
Dennis Thompson
Oct 17, 2025
3 min read
Cardiovascular Diseases
FDA Grants Accelerated Approval for First Treatment for Barth Syndrome
Lori Solomon
Sep 25, 2025
1 min read
Neurology
Apitegromab Improves Motor Function in Spinal Muscular Atrophy
Elana Gotkine
Aug 25, 2025
2 min read
Condition
Cystic Fibrosis: Symptoms, Treatments, Causes & More
Dr. Sandy Sufian, historian of medicine and disability at University of Illinois Chicago
Jun 24, 2025
10 min read
Blood Disorders
Menstrual Cycle Could Be Contributing To Sickle Cell Pain Events
Dennis Thompson
Apr 14, 2025
3 min read
Read More
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